Gene therapy AMT-130 slows Huntington’s progression by 75%

huntingtonsdiseasenews.com·Sep 25

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A gene therapy called AMT-130 has shown promise in slowing the progression of Huntington's disease, with some reports indicating a 75% reduction. The therapy has reportedly met its endpoints in a study, with plans for an FDA submission to follow. However, the regulatory path for the therapy is uncertain, with some outlets suggesting that the FDA has backtracked on its stance.

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Gene therapy AMT-130 slows Huntington’s progression by 75%

Full coverage

Huntington's Therapy Rides Regulatory Roller Coaster

Preliminary but promising gene therapy shows 75% reduction in Huntington's disease progression

The First Domino Falls: AMT-130 Gene Therapy Slows Huntington’s in Landmark Trial

Gene Therapy AMT-130 Meets End Points in Huntington Study; FDA Submission to Follow

In a first, a gene therapy seems to slow Huntington disease

FDA Backtracks on Huntington’s Disease Gene Therapy

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