Personalized CRISPR Therapy Successfully Treats Infant With Rare, Incurable CPS1 Deficiency

BioPharm International·May 16

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A baby with a rare and incurable disease, specifically CPS1 deficiency, has been treated with personalized CRISPR therapy. The treatment, which is reportedly the first of its kind, was administered to the infant, who is now said to be thriving. The specifics of the treatment and its potential applications to other diseases, such as HIV, are being explored, with the case documented in medical literature.

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View original report at BioPharm International ↗

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