Researchers to test gene therapy for rare diseases with a new FDA trial protocol

Medical Xpress·Nov 14

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Researchers are set to test gene therapy for rare diseases using a new FDA trial protocol. Some institutions, including UC Davis Health and a collaboration between Penn and CHOP, are involved in this effort, which aims to deliver custom gene therapies. However, the field has also been marked by a recent setback, including a child's sudden death, which may impact the research.

Full coverage

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UC Davis Health·Dec 8

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Inquirer.com·Nov 13

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National Institutes of Health (NIH) | (.gov)·Jun 3

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