Gene-editing therapy made in just 6 months helps baby with life-threatening disease

Science | AAAS·May 15

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A baby with a life-threatening, rare disease has been treated with a personalized gene-editing therapy made in six months. The therapy, which is reportedly the first of its kind, has been successful, with the baby now thriving and even taking steps. The treatment, which utilized CRISPR gene editing, was administered at Children's Hospital of Philadelphia.

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View original report at Science | AAAS ↗

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