Successful World First: Baby Treated with Personalized CRISPR Gene Therapy for Rare Disease is Now ‘Thriving’

Good News Network·Feb 3

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A baby with a rare genetic disease has been treated with personalized CRISPR gene therapy, reportedly with positive results. The treatment, which was developed through a collaboration between the Children's Hospital of Philadelphia and Penn Medicine, is considered a world first. The baby's condition and current status are described as improved, with some outlets stating the baby is "thriving" and has been discharged.

Full coverage

Children’s Hospital of Philadelphia Marks One-Year Anniversary of World’s First Personalized CRISPR Gene Therapy for Child with Rare Genetic Disease

Children's Hospital of Philadelphia·Feb 24

World’s first patient treated with personalized CRISPR gene editing therapy through CHOP and Penn Med collaboration

Penn Today·May 15

World’s first personalized CRISPR therapy given to baby with genetic disease

Nature·May 15

First Personalized CRISPR Gene Editing Therapy Patient Baby KJ Discharged

Inside Precision Medicine·Jun 3

Gene-editing therapy made in just 6 months helps baby with life-threatening disease

Science | AAAS·May 15

Infant becomes world's first patient to undergo personalized gene-editing treatment

CBS News·May 15

A promising genetic treatment tailor-made for a baby born with a rare disorder

NPR·May 15

Baby Is Healed With World’s First Personalized Gene-Editing Treatment (Published 2025)

The New York Times·May 15

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