Researchers have developed a patient-tailored CRISPR gene editing therapy that has been used to treat a baby with a rare and life-threatening disease. The therapy, which was created in a relatively short period of time, has shown promise in treating the infant's condition. The researchers behind this breakthrough have been recognized for their work, including being named to a list of the most influential people in the world, and are now planning to launch a new clinical trial to test the therapy for other rare diseases.